A Huntington’s Disease Treatment Is Closer Than Ever

Gene therapy is becoming a powerful way to treat challenging diseases that don’t respond to traditional treatments, and researchers now report the first success in modifying genes to slow Huntington’s disease. In a study reported by Uniqure, which developed the experimental gene therapy, scientists found that it slowed progression of Huntington’s disease by 75% over … Read more

Huntington’s disease breakthrough: what to know about the gene therapy

The caudate nucleus is one of the brain regions the gene therapy targets ONLY/SCIENCE PHOTO LIBRARY An experimental gene therapy has become the first treatment to successfully slow the progression of Huntington’s disease. While the findings are still preliminary, the approach could be a major breakthrough and may even lead to new therapies for other … Read more